We have an international reputation for undertaking pioneering clinical rare disease research. We work with many stakeholders, including charities, businesses, health organizations, and other universities, in the delivery of effective innovative and research-based solutions.
These partnerships help us accelerate positive change for families, patients, carers, researchers, health care professionals, the local health departments and member charities.
We are particularly grateful to those charities, agencies and organizations who help fund our work. We thank you.
Alberta University
Partner information

Basic Science
Partner information
Dr Viktoria Venglovecz

Dumonceaux Laboratory
Partner information
- Professor Julie Dumonceaux
- Dumonceaux Laboratory

Memorial Sloan Kettering Cancer Center
Partner information
- Dr Ross Levine, Memorial Sloan Kettering Cancer Center, New York

MiNA Therapeutics
Partner information

Newcastle University
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Queen's University Belfast
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Sorbonne University
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Tours University and Tours Hospital
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University of Liverpool
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University College Dublin
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Charities and Funders
Association of British Neurologists
Funder information

ARSLA
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Cystic Fibrosis
Funder information

Children’s Cancer and Leukaemia Group (CCLG)
Funder information

IICN - Irish Institute of Clinical Neuroscience
Funder information

IICN - Irish Institute of Clinical Neuroscience
Funder information

TargetALS
Funder information
