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We have an international reputation for undertaking pioneering clinical rare disease research. We work with many stakeholders, including charities, businesses, health organizations, and other universities, in the delivery of effective innovative and research-based solutions.

These partnerships help us accelerate positive change for families, patients, carers, researchers, health care professionals, the local health departments and member charities.

We are particularly grateful to those charities, agencies and organizations who help fund our work.  We thank you.

Alberta University

Alberta University

Partner information

Professor Toshifumi Yokota

Basic Science

Basic Science

Partner information

Dr Viktoria Venglovecz

Dumonceaux Laboratory

Dumonceaux Laboratory

Memorial Sloan Kettering Cancer Center

Memorial Sloan Kettering Cancer Center

Partner information

MiNA Therapeutics

MiNA Therapeutics

Partner information

Newcastle University

Newcastle University

Partner information

Queen's University Belfast

Queen's University Belfast

Partner information

University of Liverpool

University of Liverpool

Partner information

University College Dublin

University College Dublin

Partner information


Charities and Funders

Association of British Neurologists

Association of British Neurologists

Funder information

ARSLA

ARSLA

Funder information

Cystic Fibrosis

Cystic Fibrosis

Funder information

Children’s Cancer and Leukaemia Group (CCLG)

Children’s Cancer and Leukaemia Group (CCLG)

Funder information

IICN - Irish Institute of Clinical Neuroscience

IICN - Irish Institute of Clinical Neuroscience

Funder information

IICN - Irish Institute of Clinical Neuroscience

IICN - Irish Institute of Clinical Neuroscience

Funder information

TargetALS

TargetALS

Funder information